In a major advancement in the field of gene therapy for rare and devastating diseases, researchers have developed a "dimmer switch" system that can control levels of proteins expressed from gene therapy vectors. The system is based on alternative RNA splicing using an orally available small molecule and works effectively in tissues throughout the body, including the brain.
from Latest Science News -- ScienceDaily https://www.sciencedaily.com/releases/2021/07/210728111307.htm
from Latest Science News -- ScienceDaily https://www.sciencedaily.com/releases/2021/07/210728111307.htm
Researchers develop 'dimmer switch' to help control gene therapy
![Researchers develop 'dimmer switch' to help control gene therapy]()
Reviewed by cmakigo
on
July 29, 2021
Rating:
No comments:
Post a Comment